Medpage Today on MSN1d
First-Ever Prenatal Treatment for Spinal Muscular Atrophy Shows Promise
The first prenatal therapy for spinal muscular atrophy (SMA) showed promising results, a case report indicated. More than 2 ...
EurekAlert!1d
Promising results from first prenatal therapy for spinal muscular atrophy
Scientists at St. Jude Children’s Research Hospital report results from a promising new approach to treat the rare ...
health.wusf.usf.edu2d
Price of love: Gene therapy gives hope to a child with spinal muscular atrophy
On this episode, an infant with a harrowing diagnosis defies all odds after receiving a $2 million genetic treatment. Then, a ...
FDA approves tablet form of Evrysdi for spinal muscular atrophy
The U.S. Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for ...
abc7NY2d
LI girl speaks out after clinical trial for Spinal Muscular Atrophy cut by President Trump
A girl on Long Island is speaking out after a clinical trial for Spinal Muscular Atrophy was cut by President Trump ...
Texas Public Radio13d
Spinal stimulation restored muscles wasted by rare genetic disorder
Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...
bernama22h
Mother Shares Struggles Caring For Three Children With Spinal Muscular Atrophy
Nurul Amirah, who lives in Kampung Gaung, Tendong, said all three of her children are diagnosed with spinal muscular atrophy ...
BioSpace5d
Roche’s Evrysdi Becomes First Pill Cleared for Spinal Muscular Atrophy
The FDA on Wednesday approved the industry’s first-ever tablet treatment for spinal muscular atrophy— Roche ’s SMN2 splicing ...
Business Wire7d
FDA Approves Genentech’s Evrysdi Tablet as First and Only Tablet for Spinal Muscular Atrophy (SMA)
Genentech and Roche are investigating more than a dozen medicines for neurological disorders, including multiple sclerosis, spinal muscular atrophy, neuromyelitis optica spectrum disorder, Alzheimer’s ...
Armed robbery in Revesby11h
First Prenatal Spinal Muscular Atrophy Therapy Shows Promise
February 19, 2025) Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists ...
FDA Approves New Tablet Form of Evrysdi for Treatment of Spinal Muscular Atrophy
About Evrysdi Evrysdi is an SMN2-splicing modifier designed to increase functional SMN protein production. With the introduction of a new tablet formulation, Evrysdi now offers an alternative ...