KRRO-110 Receives Orphan Drug Designation from U.S. FDA for Alpha-1 Antitrypsin Deficiency
KRRO-110 is the first RNA editing development candidate from Korro’s proprietary OPERA TM platform and is currently being evaluated in the Phase 1/2a REWRITE clinical study for AATD. Dosing of the ...
Ex-Twitter AI ethics lead Rumman Chowdhury is worried about Musk’s impact on the federal government
Rumman Chowdhury, ex-director of Twitter's machine ethics team, has strong words for Elon Musk and the Department of ...
The FDA Cracking Down on Compounded Weight Loss Drugs – Here’s What It Means for Telehealth Companies and Consumers
After years of weight loss drug shortages, the FDA is saying there’s now an adequate supply for most medications and they ...
Evoke Pharma, Inc. Reports Fourth Quarter and Full Year 2024 Financial Results and Provides Business Update
Q4 2024 revenue increased 24.6% over Q3 2024; Full-year 2024 revenue grew 97.8% year-over-yearStrong growth in key commercial metrics, including ...
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White House withdraws nomination for CDC director; Senate committee advances NIH, FDA picks
The White House March 13 withdrew the nomination of former Republican congressman Dave Weldon for director of the Centers for ...
FDA top lawyer resigns days after starting job
The U.S. Food and Drug Administration’s chief counsel resigned two days after her appointment, according to a Thursday announcement from the agency.  “Hilary K. Perkins has resigned from her ...
RFK Jr.’s first month as health secretary: Touting French fries and casting doubts on vaccines
Kennedy vowed to “Make America Healthy Again,” has delivered an inconsistent message that has the nation’s top infectious ...
US FDA's top lawyer Hilary Perkins resigns two days into role
The U.S. Food and Drug Administration's chief counsel, Hilary Perkins, has resigned, the federal agency said in a post on ...
Trump’s FDA and NIH picks clear committee, teeing up final Senate confirmation
The Senate Health, Education, Labor, and Pensions Committee approved Dr. Jayanta Bhattacharya’s nomination to be NIH director ...
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FDA chief counsel who defended abortion pill under Biden resigns 2 days into job
Recently selected Food and Drug Administration chief lawyer, Hilary K. Perkins, has resigned from the job, according to a post from the FDA on X.  Read More ...
Companies warn investors that DOGE’s federal cuts might hurt business
As earnings season begins, filings to the SEC point to uncertainty from the current administration as potential trouble for ...
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FDA Weathers Bait-and-Switch Storm as Staff and Sites Come and Go
Marty Makary, likely FDA commissioner under President Trump, appeared before Congress this week as the agency he’s set to lead continues to be rocked by sweeping changes and about-faces.